Intern, Endpoint Development and Strategy

UltraGenix Pharmaceutical
United States - RemotePosted 5 March 2026

Job Description

<div class="content-intro"><div><strong>Why Join Us?</strong></div> <div> </div> <div><em>Be a hero for our rare disease patients</em></div> <div><em> </em></div> <div>At Ultragenyx, we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to do. To achieve this goal, our vision is to lead the future of rare disease medicine. For us, this means going where other biopharma companies won’t go – challenging the status quo and creating a new model that advances our field so more patients and caregivers can benefit from life-changing treatments. We do this by following the science, applying a novel rapid development approach, making innovative medicines at fair and reasonable prices, and creating a collaborative ecosystem to reach patients in ways that are most meaningful for them. </div> <div> </div> <div>Our commitment and care for patients extends to our people, so culture is an essential cornerstone for Ultragenyx. We remain continuously focused on creating a supportive and inclusive environment of profound learning and growth – so employees can thrive in all areas of their lives, in and outside of work. Ultimately, we want to be an organization where we would be proud for our family, friends and children to work.</div> <div> </div> <div>If you want to have a meaningful impact, do the best work of your career, and grow a lot, both professionally and personally, come join our team<em>. </em></div></div><h3 style="text-align: left;"><strong>Position Summary:</strong></h3> <p style="text-align: left;"><em><strong>ultra</strong>impact – Make a difference for those who need it most<br></em></p> <p style="text-align: left;"><span class="NormalTextRun SCXW216338695 BCX8">This </span><span class="NormalTextRun SCXW216338695 BCX8">internship </span><span class="NormalTextRun SCXW216338695 BCX8">is a unique opportunity for </span><span class="NormalTextRun SCXW216338695 BCX8">an undergraduate </span><span class="NormalTextRun SCXW216338695 BCX8">student to </span><span class="NormalTextRun SCXW216338695 BCX8">learn </span><span class="NormalTextRun SCXW216338695 BCX8">about the use of Clinical Outcomes Assessments (COAs) </span><span class="NormalTextRun SCXW216338695 BCX8">and qualitative interviews </span><span class="NormalTextRun SCXW216338695 BCX8">to characterize the impact of rare diseases </span><span class="NormalTextRun SCXW216338695 BCX8">and the effect of interventions </span><span class="NormalTextRun SCXW216338695 BCX8">on patients and </span><span class="NormalTextRun SCXW216338695 BCX8">their </span><span class="NormalTextRun SCXW216338695 BCX8">families</span><span class="NormalTextRun SCXW216338695 BCX8">.</span><span class="NormalTextRun SCXW216338695 BCX8"> </span><span class="NormalTextRun SCXW216338695 BCX8">Final project will be </span><span class="NormalTextRun SCXW216338695 BCX8">an abstract and poster for internal presentation and submission to a rare disease conference</span><span class="NormalTextRun SCXW216338695 BCX8"> and a first draft of a manuscript for submission to a rare disease or </span><span class="NormalTextRun SCXW216338695 BCX8">pediatric journal.</span><span class="NormalTextRun SCXW216338695 BCX8"> </span></p> <h3 style="text-align: left;"><strong>Work Model: </strong></h3> <p style="text-align: left;">Remote: Officially documented as working full-time from home, with travel to Ultragenyx's offices or other locations on occasion as needed.</p> <h3 style="text-align: left;"><strong>Responsibilities:</strong></h3> <ol> <li style="line-height: 2;"><span data-contrast="auto">Conduct literature reviews to identify publications on the diagnostic journey, clinical presentation, assessment and management of children with a rare disease. </span><span data-ccp-props="{"201341983":0,"335559685":706,"335559739":200,"335559740":276,"335559991":274}"> </span></li> <li style="line-height: 2;"><span data-contrast="auto">Review intervi ... (truncated, view full listing at source)